世界血友病日丨关注「玻璃人」，正确认知血友病

[1] 国家卫生健康委办公厅.《国家卫生健康委办公厅关于开展2023年出生缺陷相关宣传日活动的通知》

[2] 中华医学会血液学分会血栓与止血学组，中国血友病协作组. 血友病诊断与治疗中国专家共识 (2013年版)[J].中华血液学杂志,2013,34(5):461-463.DOI:10.3760/CMA.J.issn.0253-2727.2013.05.02

[3] 中华医学会血液学分会血栓与止血学组，中国血友病协作组. 血友病诊断与治疗中国专家共识 (2017年版)[J].中华血液学杂志,2016,37(5):364-370. DOI:10.3760/cma.j.issn.0253-2727.2017.05.002

[4] Catherine S Manno etc. AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B.Blood.2003 Apr 15;101(8):2963-72.DOI:: 10.1182/blood-2002-10-3296.Epub 2002 Dec 19.

[5] Zhang Lei etc. Safety and activity of an engineered, liver-topic adeno-associated virus vector expressing a hyperactive Padua factor IX administered with prophylactic glucocorticoids in patients with hemophilia B:a single-centre, single-arm, phase 1,pilot trial. Lancet Haematol.2022 Jul;9(7):e504-e513